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Natural history of mevalonate kinase deficiency: a literature review

Mevalonate kinase deficiency (MKD), a very rare autosomal recessive autoinflammatory disease with multiple organ involvement, presents clinically as hyperimmunoglobulinemia D syndrome (HIDS), a less severe phenotype and more common form, and mevalonic aciduria (MVA), a more severe phenotype and rare...

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Detalles Bibliográficos
Publicado en:Pediatr Rheumatol Online J
Autor Principal: Zhang, Shumin
Formato: Artigo
Idioma:Inglês
Publicado: BioMed Central 2016
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC4855321/
https://ncbi.nlm.nih.gov/pubmed/27142780
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12969-016-0091-7
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