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Lenz-Majewski mutations in PTDSS1 affect phosphatidylinositol 4-phosphate metabolism at ER-PM and ER-Golgi junctions

Lenz-Majewski syndrome (LMS) is a rare disease characterized by complex craniofacial, dental, cutaneous, and limb abnormalities combined with intellectual disability. Mutations in the PTDSS1 gene coding one of the phosphatidylserine (PS) synthase enzymes, PSS1, were described as causative in LMS pat...

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Библиографические подробности
Опубликовано в: :Proc Natl Acad Sci U S A
Главные авторы: Sohn, Mira, Ivanova, Pavlina, Brown, H. Alex, Toth, Daniel J., Varnai, Peter, Kim, Yeun Ju, Balla, Tamas
Формат: Artigo
Язык:Inglês
Опубликовано: National Academy of Sciences 2016
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Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC4843478/
https://ncbi.nlm.nih.gov/pubmed/27044099
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.1525719113
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