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A longitudinal study of emotional adjustment, quality of life and adaptive function in attenuated MPS II

OBJECTIVES: The behavioral, adaptive and quality of life characteristics of attenuated mucopolysaccharidosis type II (MPS II) have not been well studied. Understanding changes over time in the attenuated phenotype may assist in helping achieve better outcomes in long-term function. This longitudinal...

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Dettagli Bibliografici
Pubblicato in:Mol Genet Metab Rep
Autori principali: Shapiro, Elsa G., Rudser, Kyle, Ahmed, Alia, Steiner, Robert D., Delaney, Kathleen A., Yund, Brianna, King, Kelly, Kunin-Batson, Alicia, Eisengart, Julie, Whitley, Chester B.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Elsevier 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4832084/
https://ncbi.nlm.nih.gov/pubmed/27114914
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2016.03.005
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