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Phenylketonuria (PKU): A problem solved?

Phenylketonuria (PKU) is a rare metabolic disorder characterized by impaired conversion of phenylalanine (Phe) to tyrosine. If left untreated, the resultant accumulation of excess blood Phe can cause physiological, neurological, and intellectual disabilities. The National PKU Alliance (NPKUA) conduc...

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Detalles Bibliográficos
Publicado en:Mol Genet Metab Rep
Main Authors: Brown, Christine S., Lichter-Konecki, Uta
Formato: Artigo
Idioma:Inglês
Publicado: Elsevier 2015
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC4789336/
https://ncbi.nlm.nih.gov/pubmed/27014571
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2015.12.004
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