Lanean...
CRISPR-mediated Genome Editing Restores Dystrophin Expression and Function in mdx Mice
Duchenne muscular dystrophy (DMD) is a degenerative muscle disease caused by genetic mutations that lead to the disruption of dystrophin in muscle fibers. There is no curative treatment for this devastating disease. Clustered regularly interspaced short palindromic repeat/Cas9 (CRISPR/Cas9) has emer...
Gorde:
| Argitaratua izan da: | Mol Ther |
|---|---|
| Egile Nagusiak: | , , , , , , , , |
| Formatua: | Artigo |
| Hizkuntza: | Inglês |
| Argitaratua: |
Nature Publishing Group
2016
|
| Gaiak: | |
| Sarrera elektronikoa: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4786912/ https://ncbi.nlm.nih.gov/pubmed/26449883 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2015.192 |
| Etiketak: |
Etiketa erantsi
Etiketarik gabe, Izan zaitez lehena erregistro honi etiketa jartzen!
|