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Mucopolysaccharidosis IIIB confers enhanced neonatal intracranial transduction by AAV8 but not by 5, 9 or rh10

Sanfilippo syndrome type B (mucopolysaccharidosis IIIB, MPS IIIB) is a lysosomal storage disease resulting from deficiency of N-acetyl-glucosaminidase (NAGLU) activity. To determine the possible therapeutic utility of recombinant adeno-associated virus (rAAV) in early gene therapy-based intervention...

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Detalhes bibliográficos
Publicado no:Gene Ther
Main Authors: Gilkes, J A, Bloom, M D, Heldermon, C D
Formato: Artigo
Idioma:Inglês
Publicado em: Nature Publishing Group 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4777635/
https://ncbi.nlm.nih.gov/pubmed/26674264
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/gt.2015.111
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