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Mechanistic principles of antisense targets for the treatment of Spinal Muscular Atrophy

Spinal muscular atrophy (SMA) is a major neurodegenerative disorder of children and infants. SMA is primarily caused by low levels of SMN protein owing to deletions or mutations of the survival motor neuron 1 (SMN1) gene. SMN2, a nearly identical copy of SMN1, fails to compensate for the loss of the...

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Publicat a:Future Med Chem
Autors principals: Singh, Natalia N., Lee, Brian M., DiDonato, Christine J., Singh, Ravindra N.
Format: Artigo
Idioma:Inglês
Publicat: 2015
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4660980/
https://ncbi.nlm.nih.gov/pubmed/26381381
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4155/fmc.15.101
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