Long-term rescue of cone photoreceptor degeneration in retinitis pigmentosa 2 (RP2)-knockout mice by gene replacement therapy

Retinal neurodegenerative diseases are especially attractive targets for gene replacement therapy, which appears to be clinically effective for several monogenic diseases. X-linked forms of retinitis pigmentosa (XLRP) are relatively severe blinding disorders, resulting from progressive photoreceptor...

Descrición completa

Gardado en:
Detalles Bibliográficos
Publicado en:Hum Mol Genet
Main Authors: Mookherjee, Suddhasil, Hiriyanna, Suja, Kaneshiro, Kayleigh, Li, Linjing, Li, Yichao, Li, Wei, Qian, Haohua, Li, Tiansen, Khanna, Hemant, Colosi, Peter, Swaroop, Anand, Wu, Zhijian
Formato: Artigo
Idioma:Inglês
Publicado: Oxford University Press 2015
Assuntos:
Articles
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC4626763/
https://ncbi.nlm.nih.gov/pubmed/26358772
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddv354
Tags: Engadir etiqueta
Sen Etiquetas, Sexa o primeiro en etiquetar este rexistro!

Títulos similares