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Preventive study in subjects at risk of fatal familial insomnia: Innovative approach to rare diseases

The text describes a preventive clinical trial with drug treatment in a very rare neurodegenerative disease (Fatal familial Insomnia, FFI) designed with the help of individuals at genetic risk of developing the disease, asymptomatic carriers, who have agreed to be exposed over a 10-year period to do...

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Dettagli Bibliografici
Pubblicato in:Prion
Autori principali: Forloni, Gianluigi, Tettamanti, Mauro, Lucca, Ugo, Albanese, Yasmin, Quaglio, Elena, Chiesa, Roberto, Erbetta, Alessandra, Villani, Flavio, Redaelli, Veronica, Tagliavini, Fabrizio, Artuso, Vladimiro, Roiter, Ignazio
Natura: Artigo
Lingua:Inglês
Pubblicazione: Taylor & Francis 2015
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4601344/
https://ncbi.nlm.nih.gov/pubmed/25996399
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1080/19336896.2015.1027857
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