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Modifier Genes and their effect on Duchenne Muscular Dystrophy

PURPOSE OF REVIEW: Recently, genetic pathways that modify the clinical severity of Duchenne Muscular Dystrophy have been identified. The pathways uncovered as modifiers are useful to predict prognosis and also elucidate molecular signatures that can be manipulated therapeutically. RECENT FINDINGS: M...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Curr Opin Neurol
Egile Nagusiak: Vo, Andy H., McNally, Elizabeth M.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2015
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC4591871/
https://ncbi.nlm.nih.gov/pubmed/26263473
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/WCO.0000000000000240
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