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AB042. Therapies for the bone in mucopolysaccharidoses

Patients with mucopolysaccharidoses (MPS) have accumulation of glycosaminoglycans in multiple tissues which may cause coarse facial features, mental retardation, recurrent ear and nose infections, inguinal and umbilical hernias, hepatosplenomegaly, and skeletal deformities. Clinical features related...

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Detalles Bibliográficos
Publicado en:Ann Transl Med
Autor Principal: Tomatsu, Shunji
Formato: Artigo
Idioma:Inglês
Publicado: AME Publishing Company 2015
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC4563430/
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3978/j.issn.2305-5839.2015.AB042
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