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Gene therapy for Mucopolysaccharidoses

Mucopolysaccharidoses (MPS) are a group of lysosomal storage disorders (LSDs) caused by a deficiency of lysosomal enzymes, leading to a wide range of various clinical symptoms depending upon the type of MPS or its severity. Enzyme replacement therapy (ERT), hematopoietic stem cell transplantation (H...

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Detalhes bibliográficos
Publicado no:Mol Genet Metab
Main Authors: Sawamoto, Kazuki, Chen, Hui-Hsuan, Alméciga-Díaz, Carlos J., Mason, Robert W., Tomatsu, Shunji
Formato: Artigo
Idioma:Inglês
Publicado em: 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5986190/
https://ncbi.nlm.nih.gov/pubmed/29295764
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgme.2017.12.434
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