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Molecular Basis of Neurodegeneration and Neurodevelopmental Defects in Menkes Disease

ATP7A mutations impair copper metabolism resulting in three distinct genetic disorders in humans. These diseases are characterized by neurological phenotypes ranging from intellectual disability to neurodegeneration. Severe ATP7A loss-of function alleles trigger Menkes disease, a copper deficiency c...

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Detalhes bibliográficos
Publicado no:Neurobiol Dis
Main Authors: Zlatic, Stephanie, Comstra, Heather Skye, Gokhale, Avanti, Petris, Michael J., Faundez, Victor
Formato: Artigo
Idioma:Inglês
Publicado em: 2015
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4499018/
https://ncbi.nlm.nih.gov/pubmed/25583185
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.nbd.2014.12.024
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