Pressure for drug development in lysosomal storage disorders – a quantitative analysis thirty years beyond the US orphan drug act

Lignende værker

• Novel orphan medicines and abandoned pathways - the US Orphan Drug Act of 1983 and the impact on rare rheumatologic diseases and lysosomal storage disorders
  af: Ries, Markus, et al.
  Udgivet: (2015)
• FDA orphan drug designations for lysosomal storage disorders – a cross-sectional analysis
  af: Garbade, Sven F., et al.
  Udgivet: (2020)
• Novel Treatments for Rare Cancers: The U.S. Orphan Drug Act Is Delivering—A Cross-Sectional Analysis
  af: Stockklausner, Clemens, et al.
  Udgivet: (2016)
• Novel treatments for rare rheumatologic disorders: analysis of the impact of 30 years of the US orphan drug act
  af: Lutz, Thomas, et al.
  Udgivet: (2016)
• Thirty Years of Orphan Drug Legislation and the Development of Drugs to Treat Rare Seizure Conditions: A Cross Sectional Analysis
  af: Döring, Jan Henje, et al.
  Udgivet: (2016)