Pressure for drug development in lysosomal storage disorders – a quantitative analysis thirty years beyond the US orphan drug act

Por Mechler, Konstantin, Mountford, William K, Hoffmann, Georg F, Ries, Markus
Publicado no Orphanet J Rare Dis (2015)

Novel orphan medicines and abandoned pathways - the US Orphan Drug Act of 1983 and the impact on rare rheumatologic diseases and lysosomal storage disorders

Por Ries, Markus, Lutz, Thomas, Lampert, Anette, Mountford, William, Mechler, Konstantin, Hoffmann, Georg F
Publicado no Mol Cell Pediatr (2015)

Glutamatergic medication in the treatment of obsessive compulsive disorder (OCD) and autism spectrum disorder (ASD) – study protocol for a randomised controlled trial

Por Häge, Alexander, Banaschewski, Tobias, Buitelaar, Jan K., Dijkhuizen, Rick M., Franke, Barbara, Lythgoe, David J., Mechler, Konstantin, Williams, Steven C. R., Dittmann, Ralf W.
Publicado no Trials (2016)