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Positive effect of erythrocyte-delivered dexamethasone in ataxia-telangiectasia
OBJECTIVE: Ataxia-telangiectasia (AT) is a rare, devastating neurodegenerative disease presenting with early-onset ataxia, oculocutaneous telangiectasia, immunodeficiency, radiosensitivity, and proneness to cancer. In a previous phase 2 study, we showed that 6 monthly infusions of autologous erythro...
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| Publicado en: | Neurol Neuroimmunol Neuroinflamm |
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| Autores principales: | , , , , , , , , , , , , , , |
| Formato: | Artigo |
| Lenguaje: | Inglês |
| Publicado: |
Lippincott Williams & Wilkins
2015
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| Materias: | |
| Acceso en línea: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4396528/ https://ncbi.nlm.nih.gov/pubmed/25884015 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/NXI.0000000000000098 |
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