Intra-Erythrocyte Infusion of Dexamethasone Reduces Neurological Symptoms in Ataxia Teleangiectasia Patients: Results of a Phase 2 Trial

BACKGROUND: Ataxia Teleangiectasia [AT] is a rare neurodegenerative disease characterized by early onset ataxia, oculocutaneous teleangiectasias, immunodeficiency, recurrent infections, radiosensitivity and proneness to cancer. No therapies are available for this devastating disease. Recent observat...

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Wedi'i Gadw mewn:
Manylion Llyfryddiaeth
Prif Awduron: Chessa, Luciana, Leuzzi, Vincenzo, Plebani, Alessandro, Soresina, Annarosa, Micheli, Roberto, D’Agnano, Daniela, Venturi, Tullia, Molinaro, Anna, Fazzi, Elisa, Marini, Mirella, Ferremi Leali, Pierino, Quinti, Isabella, Cavaliere, Filomena Monica, Girelli, Gabriella, Pietrogrande, Maria Cristina, Finocchi, Andrea, Tabolli, Stefano, Abeni, Damiano, Magnani, Mauro
Fformat: Artigo
Iaith:Inglês
Cyhoeddwyd: BioMed Central 2014
Pynciau:
Research
Mynediad Ar-lein:https://ncbi.nlm.nih.gov/pmc/articles/PMC3904207/
https://ncbi.nlm.nih.gov/pubmed/24405665
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1750-1172-9-5
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