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Hybrid Nonviral/Viral Vector Systems for Improved piggyBac DNA Transposon In Vivo Delivery

The DNA transposon piggyBac is a potential therapeutic agent for multiple genetic diseases such as cystic fibrosis (CF). Recombinant piggyBac transposon and transposase are typically codelivered by plasmid transfection; however, plasmid delivery is inefficient in somatic cells in vivo and is a barri...

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Bibliografiset tiedot
Julkaisussa:Mol Ther
Päätekijät: Cooney, Ashley L, Singh, Brajesh K, Sinn, Patrick L
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Nature Publishing Group 2015
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC4395777/
https://ncbi.nlm.nih.gov/pubmed/25557623
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2014.254
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