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Brain white matter volume abnormalities in Lesch-Nyhan disease and its variants

OBJECTIVE: We sought to examine brain white matter abnormalities based on MRI in adults with Lesch-Nyhan disease (LND) or an attenuated variant (LNV) of this rare, X-linked neurodevelopmental disorder of purine metabolism. METHODS: In this observational study, we compared 21 adults with LND, 17 with...

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Dades bibliogràfiques
Publicat a:Neurology
Autors principals: Schretlen, David J., Varvaris, Mark, Vannorsdall, Tracy D., Gordon, Barry, Harris, James C., Jinnah, H.A.
Format: Artigo
Idioma:Inglês
Publicat: Lippincott Williams & Wilkins 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4336080/
https://ncbi.nlm.nih.gov/pubmed/25503620
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000001128
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