載入...

Minimal Ureagenesis is Necessary for Survival in the Murine Model of Hyperargininemia Treated by AAV-based Gene Therapy

Hyperammonemia is less severe in arginase 1 deficiency compared with other urea cycle defects. Affected patients manifest hyperargininemia and infrequent episodes of hyperammonemia. Patients typically suffer from neurological impairment with cortical and pyramidal tract deterioration, spasticity, lo...

全面介紹

Na minha lista:
書目詳細資料
發表在:Gene Ther
Main Authors: Hu, Chuhong, Tai, Denise S., Park, Hana, Cantero-Nieto, Gloria, Chan, Emily, Yudkoff, Marc, Cederbaum, Stephen D., Lipshutz, Gerald S.
格式: Artigo
語言:Inglês
出版: 2014
主題:
在線閱讀:https://ncbi.nlm.nih.gov/pmc/articles/PMC4320015/
https://ncbi.nlm.nih.gov/pubmed/25474440
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/gt.2014.106
標簽: 添加標簽
沒有標簽, 成為第一個標記此記錄!