載入...

Spinal muscular atrophy: from tissue specificity to therapeutic strategies

Spinal muscular atrophy (SMA) is the most frequent genetic cause of death in infants and toddlers. All cases of spinal muscular atrophy result from reductions in levels of the survival motor neuron (SMN) protein, and so SMN upregulation is a focus of many preclinical and clinical studies. We examine...

全面介紹

Na minha lista:
書目詳細資料
發表在:F1000Prime Rep
Main Authors: Iascone, Daniel M., Henderson, Christopher E., Lee, Justin C.
格式: Artigo
語言:Inglês
出版: Faculty of 1000 Ltd 2015
主題:
在線閱讀:https://ncbi.nlm.nih.gov/pmc/articles/PMC4311279/
https://ncbi.nlm.nih.gov/pubmed/25705387
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.12703/P7-04
標簽: 添加標簽
沒有標簽, 成為第一個標記此記錄!