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Rubinstein-Taybi syndrome: clinical features, genetic basis, diagnosis, and management

BACKGROUND: Rubinstein-Taybi syndrome (RSTS) is an extremely rare autosomal dominant genetic disease, with an estimated prevalence of one case per 125,000 live births. RSTS is characterized by typical facial features, microcephaly, broad thumbs and first toes, intellectual disability, and postnatal...

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Dades bibliogràfiques
Publicat a:Ital J Pediatr
Autors principals: Milani, Donatella, Manzoni, Francesca Maria Paola, Pezzani, Lidia, Ajmone, Paola, Gervasini, Cristina, Menni, Francesca, Esposito, Susanna
Format: Artigo
Idioma:Inglês
Publicat: BioMed Central 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4308897/
https://ncbi.nlm.nih.gov/pubmed/25599811
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13052-015-0110-1
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