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Fetal Globin Induction—Can It Cure β Thalassemia?

The β thalassemias are one of a few medical conditions in which reactivation of a gene product that is expressed during fetal life can functionally replace a deficiency of essential proteins expressed at a later developmental stage. The fetal globin genes are present and normally integrated in hemat...

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Dettagli Bibliografici
Pubblicato in:Hematology Am Soc Hematol Educ Program
Autore principale: Perrine, Susan P.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2005
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4262245/
https://ncbi.nlm.nih.gov/pubmed/16304357
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/asheducation-2005.1.38
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