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Clinical, Biochemical, and Molecular Presentation in a Patient with the cblD-Homocystinuria Inborn Error of Cobalamin Metabolism

Disorders of intracellular cobalamin (vitamin B(12)) metabolism result from deficient synthesis of the coenzymes derived from vitamin B(12): adenosylcobalamin and methylcobalamin. Disturbances of cobalamin-cofactor synthesis result in elevated levels of homocysteine and/or methylmalonic acid. Nine d...

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Dades bibliogràfiques
Publicat a:JIMD Rep
Autors principals: Atkinson, Celia, Miousse, Isabelle R., Watkins, David, Rosenblatt, David S., Raiman, Julian A. J.
Format: Artigo
Idioma:Inglês
Publicat: Springer Berlin Heidelberg 2014
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4241196/
https://ncbi.nlm.nih.gov/pubmed/25155779
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2014_340
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