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Metallothioneins as dynamic markers for brain disease in lysosomal disorders

OBJECTIVE: To facilitate development of novel disease-modifying therapies for lysosomal storage disorder (LSDs) characterized by nervous system involvement such as metachromatic leukodystrophy (MLD), molecular markers for monitoring disease progression and therapeutic response are needed. To this en...

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Detalhes bibliográficos
Publicado no:Ann Neurol
Main Authors: Cesani, Martina, Cavalca, Eleonora, Macco, Romina, Leoncini, Giuseppe, Terreni, Maria Rosa, Lorioli, Laura, Furlan, Roberto, Comi, Giancarlo, Doglioni, Claudio, Zacchetti, Daniele, Sessa, Maria, Scherzer, Clemens R, Biffi, Alessandra
Formato: Artigo
Idioma:Inglês
Publicado em: BlackWell Publishing Ltd 2014
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4237725/
https://ncbi.nlm.nih.gov/pubmed/24242821
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ana.24053
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