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Metallothioneins as dynamic markers for brain disease in lysosomal disorders

OBJECTIVE: To facilitate development of novel disease-modifying therapies for lysosomal storage disorder (LSDs) characterized by nervous system involvement such as metachromatic leukodystrophy (MLD), molecular markers for monitoring disease progression and therapeutic response are needed. To this en...

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Dettagli Bibliografici
Pubblicato in:Ann Neurol
Autori principali: Cesani, Martina, Cavalca, Eleonora, Macco, Romina, Leoncini, Giuseppe, Terreni, Maria Rosa, Lorioli, Laura, Furlan, Roberto, Comi, Giancarlo, Doglioni, Claudio, Zacchetti, Daniele, Sessa, Maria, Scherzer, Clemens R, Biffi, Alessandra
Natura: Artigo
Lingua:Inglês
Pubblicazione: BlackWell Publishing Ltd 2014
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4237725/
https://ncbi.nlm.nih.gov/pubmed/24242821
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ana.24053
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