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Metallothioneins as dynamic markers for brain disease in lysosomal disorders

OBJECTIVE: To facilitate development of novel disease-modifying therapies for lysosomal storage disorder (LSDs) characterized by nervous system involvement such as metachromatic leukodystrophy (MLD), molecular markers for monitoring disease progression and therapeutic response are needed. To this en...

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Vydáno v:Ann Neurol
Hlavní autoři: Cesani, Martina, Cavalca, Eleonora, Macco, Romina, Leoncini, Giuseppe, Terreni, Maria Rosa, Lorioli, Laura, Furlan, Roberto, Comi, Giancarlo, Doglioni, Claudio, Zacchetti, Daniele, Sessa, Maria, Scherzer, Clemens R, Biffi, Alessandra
Médium: Artigo
Jazyk:Inglês
Vydáno: BlackWell Publishing Ltd 2014
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC4237725/
https://ncbi.nlm.nih.gov/pubmed/24242821
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ana.24053
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