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Isolated Mild Intellectual Disability Expands the Aminoacylase 1 Phenotype Spectrum

Aminoacylase 1 (ACY1) deficiency is a rare inborn error of metabolism presenting with heterogeneous neurological symptoms such as psychomotor delay, seizures, intellectual disability and it is characterized by increased urinary excretion of N-acetylated amino acids. We report on a new patient who pr...

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Publicat a:JIMD Rep
Autors principals: Alessandrì, Maria G., Casarano, Manuela, Pezzini, Ilaria, Doccini, Stefano, Nesti, Claudia, Cioni, Giovanni, Battini, Roberta
Format: Artigo
Idioma:Inglês
Publicat: Springer Berlin Heidelberg 2014
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4221304/
https://ncbi.nlm.nih.gov/pubmed/24997716
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2014_323
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