A carregar...

Fifteen-year follow-up of Italian families affected by arginine glycine amidinotransferase deficiency

BACKGROUND: Arginine:glycine amidinotransferase deficiency (AGAT-d) is a very rare inborn error of creatine synthesis mainly characterized by absence of brain Creatine (Cr) peak, intellectual disability, severe language impairment and behavioural disorder and susceptible to supplementary Cr treatmen...

ver descrição completa

Na minha lista:
Detalhes bibliográficos
Publicado no:Orphanet J Rare Dis
Main Authors: Battini, Roberta, Alessandrì, M. Grazia, Casalini, Claudia, Casarano, Manuela, Tosetti, Michela, Cioni, Giovanni
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5289057/
https://ncbi.nlm.nih.gov/pubmed/28148286
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-017-0577-5
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!