Cargando...

Laronidase Replacement Therapy and Left Ventricular Function in Mucopolysaccharidosis I

We assessed the effects of long-term laronidase replacement therapy (LRT) on the left ventricular (LV) function of a 52-year-old adult woman with mucopolysaccharidosis I (MPS I). The urinary uronic acid concentration significantly decreased by 78.7% (from 75 to 16 mg/g creatinine) after LRT; thereaf...

Descrición completa

Gardado en:
Detalles Bibliográficos
Publicado en:JIMD Rep
Main Authors: Harada, Haruhito, Niiyama, Hiroshi, Katoh, Atsushi, Ikeda, Hisao
Formato: Artigo
Idioma:Inglês
Publicado: Springer Berlin Heidelberg 2014
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC4221302/
https://ncbi.nlm.nih.gov/pubmed/24850236
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2014_316
Tags: Engadir etiqueta
Sen Etiquetas, Sexa o primeiro en etiquetar este rexistro!