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The therapeutic potential of chemical chaperones in protein folding diseases

Several neurodegenerative diseases are caused by defects in protein folding, including Alzheimer, Parkinson, Huntington, and prion diseases. Once a disease-specific protein misfolds, it can then form toxic aggregates which accumulate in the brain, leading to neuronal dysfunction, cell death, and cli...

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Autors principals: Cortez, Leonardo, Sim, Valerie
Format: Artigo
Idioma:Inglês
Publicat: Landes Bioscience 2014
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4189890/
https://ncbi.nlm.nih.gov/pubmed/24818993
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4161/pri.28938
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