Loading...
Defining the therapeutic window in a severe animal model of spinal muscular atrophy
Spinal muscular atrophy (SMA) is a neurodegenerative disease caused by the loss of a single gene, Survival Motor Neuron-1 (SMN1). Administration of a self-complementary Adeno-Associated Virus vector expressing full-length SMN cDNA (scAAV-SMN) has proven an effective means to rescue the SMA phenotype...
Na minha lista:
| Main Authors: | , , , , |
|---|---|
| Format: | Artigo |
| Sprog: | Inglês |
| Udgivet: |
Oxford University Press
2014
|
| Fag: | |
| Online adgang: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4119406/ https://ncbi.nlm.nih.gov/pubmed/24722206 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddu169 |
| Tags: |
Tilføj Tag
Ingen Tags, Vær først til at tagge denne postø!
|