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Chemical chaperone ameliorates pathological protein aggregation in plectin-deficient muscle

The ubiquitously expressed multifunctional cytolinker protein plectin is essential for muscle fiber integrity and myofiber cytoarchitecture. Patients suffering from plectinopathy-associated epidermolysis bullosa simplex with muscular dystrophy (EBS-MD) and mice lacking plectin in skeletal muscle dis...

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Detalhes bibliográficos
Main Authors: Winter, Lilli, Staszewska, Ilona, Mihailovska, Eva, Fischer, Irmgard, Goldmann, Wolfgang H., Schröder, Rolf, Wiche, Gerhard
Formato: Artigo
Idioma:Inglês
Publicado em: American Society for Clinical Investigation 2014
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3934181/
https://ncbi.nlm.nih.gov/pubmed/24487589
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI71919
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