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Telomere phenotypes in females with heterozygous mutations in the dyskeratosis congenita 1 (DKC1) gene

Dyskeratosis congenita is a telomere-mediated syndrome defined by mucocutaneous features. The X-linked mode of inheritance accounts for half the cases, and is thought to predominantly manifest in childhood as bone marrow failure. We identified two male probands who presented in the fifth decade with...

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Autors principals: Alder, Jonathan K., Parry, Erin M., Yegnasubramanian, Srinivasan, Wagner, Christa L., Lieblich, Lawrence M., Auerbach, Robert, Auerbach, Arleen D., Wheelan, Sarah J., Armanios, Mary
Format: Artigo
Idioma:Inglês
Publicat: 2013
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3926107/
https://ncbi.nlm.nih.gov/pubmed/23946118
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/humu.22397
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