Caricamento...

Treatment of Smith-Lemli-Opitz Syndrome and Other Sterol Disorders

Smith-Lemli-Opitz syndrome (SLOS) is an autosomal recessive genetic condition with a broad phenotype that results from deficiency of the final enzyme of the cholesterol synthesis pathway. This defect causes low or low-normal plasma cholesterol levels and increased 7- and 8-dehydrocholesterol (DHC) l...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Autori principali: Svoboda, Melissa D., Christie, Jill M., Eroglu, Yasemen, Freeman, Kurt A., Steiner, Robert D.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2012
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3890258/
https://ncbi.nlm.nih.gov/pubmed/23042642
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ajmg.c.31347
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne! !