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Altered expression and splicing of Ca(2+) metabolism genes in myotonic dystrophies DM1 and DM2

AIMS: Myotonic dystrophy types 1 and 2 (DM1 and DM2) are multisystem disorders caused by similar repeat expansion mutations, with similar yet distinct clinical features. Aberrant splicing of multiple effector genes, as well as dysregulation of transcription and translation, have been suggested to un...

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Autors principals: Vihola, Anna, Sirito, Mario, Bachinski, Linda L., Raheem, Olayinka, Screen, Mark, Suominen, Tiina, Krahe, Ralf, Udd, Bjarne
Format: Artigo
Idioma:Inglês
Publicat: 2013
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3882430/
https://ncbi.nlm.nih.gov/pubmed/22758909
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/j.1365-2990.2012.01289.x
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