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Longitudinal quality of life analysis in a phenylketonuria cohort provided sapropterin dihydrochloride

BACKGROUND: Sapropterin dihydrochloride effectively lowers plasma phenylalanine (Phe) for at least a third of phenylketonuria (PKU) patients, with potential for increased dietary Phe tolerance and decreased medical food requirement. OBJECTIVE: To investigate long-term quality of life (QOL) in patien...

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Autores principales: Douglas, Teresa D, Ramakrishnan, Usha, Kable, Julie A, Singh, Rani H
Formato: Artigo
Lenguaje:Inglês
Publicado: BioMed Central 2013
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC3880979/
https://ncbi.nlm.nih.gov/pubmed/24373161
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1477-7525-11-218
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