Загрузка...
Longitudinal quality of life analysis in a phenylketonuria cohort provided sapropterin dihydrochloride
BACKGROUND: Sapropterin dihydrochloride effectively lowers plasma phenylalanine (Phe) for at least a third of phenylketonuria (PKU) patients, with potential for increased dietary Phe tolerance and decreased medical food requirement. OBJECTIVE: To investigate long-term quality of life (QOL) in patien...
Сохранить в:
| Главные авторы: | , , , |
|---|---|
| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
BioMed Central
2013
|
| Предметы: | |
| Online-ссылка: | https://ncbi.nlm.nih.gov/pmc/articles/PMC3880979/ https://ncbi.nlm.nih.gov/pubmed/24373161 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1477-7525-11-218 |
| Метки: |
Добавить метку
Нет меток, Требуется 1-ая метка записи!
|