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Novel Deletion Mutation Identified in a Patient with Late-Onset Combined Methylmalonic Acidemia and Homocystinuria, cblC Type

Combined methylmalonic aciduria and homocystinuria, cblC type (MMACHC), is the most common inborn error of cellular vitamin B(12) metabolism and is caused by mutations in the MMACHC gene. This metabolic disease results in impaired intracellular synthesis of adenosylcobalamin and methylcobalamin, coe...

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Библиографические подробности
Главные авторы: Backe, Paul Hoff, Ytre-Arne, Mari, Røhr, Åsmund Kjendseth, Brodtkorb, Else, Fowler, Brian, Rootwelt, Helge, Bjørås, Magnar, Mørkrid, Lars
Формат: Artigo
Язык:Inglês
Опубликовано: Springer Berlin Heidelberg 2013
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC3755550/
https://ncbi.nlm.nih.gov/pubmed/23580368
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2013_225
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