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SMN-inducing compounds for the treatment of spinal muscular atrophy

Spinal muscular atrophy (SMA) is a leading genetic cause of infant mortality. A neurodegenerative disease, it is caused by loss of SMN1, although low, but essential, levels of SMN protein are produced by the nearly identical gene SMN2. While no effective treatment or therapy currently exists, a new...

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Detalles Bibliográficos
Main Authors: Lorson, Monique A, Lorson, Christian L
Formato: Artigo
Idioma:Inglês
Publicado: 2012
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC3589915/
https://ncbi.nlm.nih.gov/pubmed/23157239
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4155/fmc.12.131
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