Enzyme replacement is associated with better cognitive outcomes after transplant in Hurler syndrome

OBJECTIVE: To investigate whether intravenous enzyme replacement therapy (ERT) benefits cognitive function in patients with mucopolysaccharidosis Type IH (Hurler syndrome, MPS IH) undergoing hematopoietic cell transplantation (HCT). STUDY DESIGN: Data were obtained for nine children treated with HCT...

Cijeli opis

Spremljeno u:
Bibliografski detalji
Glavni autori: Eisengart, Julie B., Rudser, Kyle D., Tolar, Jakub, Orchard, Paul J., Kivisto, Teresa, Ziegler, Richard S., Whitley, Chester, Shapiro, Elsa
Format: Artigo
Jezik:Inglês
Izdano: 2012
Teme:
Article
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC3524404/
https://ncbi.nlm.nih.gov/pubmed/22974573
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.jpeds.2012.07.052
Oznake: Dodaj oznaku
Bez oznaka, Budi prvi tko označuje ovaj zapis!

Similar Items