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Long-term eculizumab improves clinical outcomes in atypical hemolytic uremic syndrome

BACKGROUND: Atypical hemolytic uremic syndrome (aHUS) is a rare genetic disorder caused by chronic uncontrolled complement activation. CASE-DIAGNOSIS/TREATMENT: We present a 4-year-old girl with aHUS who had multiple severe clinical manifestations of thrombotic microangiopathy (TMA) including acute...

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Autori principali: Vilalta, Ramon, Lara, Enrique, Madrid, Alvaro, Chocron, Sara, Muñoz, Marina, Casquero, Alex, Nieto, Jose
Natura: Artigo
Lingua:Inglês
Pubblicazione: Springer-Verlag 2012
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3491201/
https://ncbi.nlm.nih.gov/pubmed/22890512
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s00467-012-2276-8
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