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Analysis of a read-through promoting compound in a severe mouse model of Spinal Muscular Atrophy

Spinal Muscular Atrophy (SMA) is the leading genetic cause of infantile death and caused by the loss of functional Survival Motor Neuron 1(SMN1). The remaining copy gene, SMN2, is unable to rescue from disease because the primary gene product lacks the final coding exon, exon 7, due to an alternativ...

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Bibliografiske detaljer
Main Authors: Mattis, Virginia B., Chang, Cheng-Wei Tom, Lorson, Christian L.
Format: Artigo
Sprog:Inglês
Udgivet: 2012
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC3426503/
https://ncbi.nlm.nih.gov/pubmed/22819971
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.neulet.2012.07.024
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