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Myoclonus-dystonia syndrome due to tyrosine hydroxylase deficiency

OBJECTIVE: To present a new family with tyrosine hydroxylase deficiency (THD) that presented with a new phenotype of predominant, levodopa-responsive myoclonus with dystonia due to compound heterozygosity of one previously reported mutation in the promoter region and a novel nonsynonymous mutation i...

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Hlavní autoři: Stamelou, Maria, Mencacci, Niccolo E., Cordivari, Carla, Batla, Amit, Wood, Nick W., Houlden, Henry, Hardy, John, Bhatia, Kailash P.
Médium: Artigo
Jazyk:Inglês
Vydáno: Lippincott Williams & Wilkins 2012
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC3405253/
https://ncbi.nlm.nih.gov/pubmed/22815559
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0b013e318261714a
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