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Molecular Chaperones as Targets to Circumvent the CFTR Defect in Cystic Fibrosis

Cystic Fibrosis (CF) is the most common autosomal recessive lethal disorder among Caucasian populations. CF results from mutations and resulting dysfunction of the Cystic Fibrosis Transmembrane Conductance Regulator (CFTR). CFTR is a cyclic AMP-dependent chloride channel that is localized to the api...

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Autors principals: Chanoux, Rebecca A., Rubenstein, Ronald C.
Format: Artigo
Idioma:Inglês
Publicat: Frontiers Research Foundation 2012
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3398409/
https://ncbi.nlm.nih.gov/pubmed/22822398
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fphar.2012.00137
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