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Cysteamine therapy: a treatment for cystinosis, not a cure

Cystinosis as a clinical entity is a progressive dysfunction of multiple organs caused by the accumulation of cystine in the tissues, leading, for example, to end-stage renal failure, diabetes, hypothyroidism, myopathy, and central nervous system deterioration. Brodin-Sartorius and colleagues presen...

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Autore principale: Cherqui, Stephanie
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2012
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3386783/
https://ncbi.nlm.nih.gov/pubmed/22205430
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/ki.2011.301
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