Rescue of bilirubin-induced neonatal lethality in a mouse model of Crigler-Najjar syndrome type I by AAV9-mediated gene transfer

Lignende værker

• Life-Long Correction of Hyperbilirubinemia with a Neonatal Liver-Specific AAV-Mediated Gene Transfer in a Lethal Mouse Model of Crigler–Najjar Syndrome
  af: Bortolussi, Giulia, et al.
  Udgivet: (2014)
• Promoterless gene targeting without nucleases rescues lethality of a Crigler‐Najjar syndrome mouse model
  af: Porro, Fabiola, et al.
  Udgivet: (2017)
• Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome
  af: Collaud, Fanny, et al.
  Udgivet: (2018)
• Unconjugated Bilirubin and an Increased Proportion of Bilirubin Monoconjugates in the Bile of Patients with Gilbert's Syndrome and Crigler-Najjar Disease
  af: Fevery, Johan, et al.
  Udgivet: (1977)
• A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome
  af: Ronzitti, Giuseppe, et al.
  Udgivet: (2016)