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Gene Therapy for Lysosomal Storage Diseases (LSDs) in Large Animal Models

Lysosomal storage diseases (LSDs) are inherited metabolic disorders caused by deficient activity of a single lysosomal enzyme or other defects resulting in deficient catabolism of large substrates in lysosomes. There are more than 40 forms of inherited LSDs known to occur in humans, with an aggregat...

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Detalhes bibliográficos
Autor principal: Haskins, Mark
Formato: Artigo
Idioma:Inglês
Publicado em: 2009
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3340575/
https://ncbi.nlm.nih.gov/pubmed/19293456
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