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Spinal muscular atrophy

Spinal muscular atrophy (SMA) is an autosomal recessive neuromuscular disease characterized by degeneration of alpha motor neurons in the spinal cord, resulting in progressive proximal muscle weakness and paralysis. Estimated incidence is 1 in 6,000 to 1 in 10,000 live births and carrier frequency o...

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Autors principals: D'Amico, Adele, Mercuri, Eugenio, Tiziano, Francesco D, Bertini, Enrico
Format: Artigo
Idioma:Inglês
Publicat: BioMed Central 2011
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3231874/
https://ncbi.nlm.nih.gov/pubmed/22047105
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1750-1172-6-71
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