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Design principles for bifunctional targeted oligonucleotide enhancers of splicing

Controlling the patterns of splicing of specific genes is an important goal in the development of new therapies. We have shown that the splicing of a refractory exon, SMN2 exon 7, could be increased in fibroblasts derived from patients with spinal muscular atrophy by using bifunctional targeted olig...

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Autori principali: Owen, Nicholas, Zhou, Haiyan, Malygin, Alexey A., Sangha, Jason, Smith, Lindsay D., Muntoni, Francesco, Eperon, Ian C.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Oxford University Press 2011
Soggetti:
RNA
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3167598/
https://ncbi.nlm.nih.gov/pubmed/21602265
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/nar/gkr152
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