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Rapamycin for treating Tuberous Sclerosis and Autism Spectrum Disorders

Tuberous sclerosis (TSC) is a genetic disorder caused by heterozygous mutations in the TSC1 or TSC2 genes and is associated with autism spectrum disorders (ASD) in 20–60% of cases. In addition, altered TSC/mTOR signaling is emerging as a feature common to a subset of ASD. Recent findings, in animal...

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Hlavní autoři: Ehninger, Dan, Silva, Alcino J.
Médium: Artigo
Jazyk:Inglês
Vydáno: 2010
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC3075964/
https://ncbi.nlm.nih.gov/pubmed/21115397
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.molmed.2010.10.002
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